Clinical observation and anti-drug antibody monitoring of enzyme replacement therapy in children with Fabry disease

Objective: To analyze the efficacy of enzyme replacement therapy and anti-drug antibody production in children with Fabry disease. Methods: The clinical data of 7 children with Fabry disease treated with enzyme replacement therapy for more than 1 year at Children's Hospital of Zhejiang Universi...

Description complète

Détails bibliographiques
Publié dans:Zhonghua er ke za zhi = Chinese journal of pediatrics. - 1960. - 63(2025), 1 vom: 02. Jan., Seite 75-79
Auteur principal: Lu, Z H (Auteur)
Autres auteurs: Shou, X Y, Lin, Q, Zhang, L X, Fu, H D, Mao, J H
Format: Article en ligne
Langue:Chinese
Publié: 2025
Accès à la collection:Zhonghua er ke za zhi = Chinese journal of pediatrics
Sujets:English Abstract Journal Article alpha-Galactosidase EC 3.2.1.22 Sphingolipids Trihexosylceramides globotriaosyl lysosphingolipid 126550-86-5 Antibodies Isoenzymes Glycolipids