Relative CD4 lymphopenia and a skewed memory phenotype are the main immunologic abnormalities in a child with Omenn syndrome due to homozygous RAG1-C2633T hypomorphic mutation

We report a child with Omenn syndrome (OS) due to homozygous RAG1-C2633T mutations who had an unusual clinical and immunological presentation. She had delayed onset of OS-associated clinical features, had cleared a number of potentially fatal pathogens including respiratory syncytial virus, parainfl...

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Veröffentlicht in:Clinical immunology (Orlando, Fla.). - 1999. - 131(2009), 3 vom: 15. Juni, Seite 447-55
1. Verfasser: McCusker, Christine (VerfasserIn)
Weitere Verfasser: Hotte, Simon, Le Deist, Francoise, Hirschfeld, Aaron F, Mitchell, David, Nguyen, Van-Hung, Gagnon, Remi, Mazer, Bruce, Turvey, Stuart E, Jabado, Nada
Format: Online-Aufsatz
Sprache:English
Veröffentlicht: 2009
Zugriff auf das übergeordnete Werk:Clinical immunology (Orlando, Fla.)
Schlagworte:Case Reports Journal Article Research Support, Non-U.S. Gov't Homeodomain Proteins RAG-1 protein 128559-51-3
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245 1 0 |a Relative CD4 lymphopenia and a skewed memory phenotype are the main immunologic abnormalities in a child with Omenn syndrome due to homozygous RAG1-C2633T hypomorphic mutation 
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520 |a We report a child with Omenn syndrome (OS) due to homozygous RAG1-C2633T mutations who had an unusual clinical and immunological presentation. She had delayed onset of OS-associated clinical features, had cleared a number of potentially fatal pathogens including respiratory syncytial virus, parainfluenza-3 virus and rotavirus, and was thriving at diagnosis. Laboratory assessment showed normal T and B lymphocyte number and function. T-cell-receptor repertoire in the blood was relatively diverse and her primary immunologic abnormality was skewing of circulating T-cells to the memory phenotype. A compelling explanation for the perplexing combination in OS of atopic/autoimmune and immunologic features has proven elusive. Homozygous RAG1-C2633T hypomorphic mutation may lead to significant residual immunity and a skewed memory phenotype. Our findings suggest that, in addition to host-genetic factors, environment, and/or pathogens, hypomorphic RAG mutations may differentially impact on V(D)J recombination activity and hence lead to a variable ability to sustain T and B cell lymphopoiesis. Importantly, this case emphasizes that such hypomorphic mutations may promote an attenuated phenotype, complicating the diagnosis of primary immunodeficiency (PID) 
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650 4 |a Journal Article 
650 4 |a Research Support, Non-U.S. Gov't 
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700 1 |a Hotte, Simon  |e verfasserin  |4 aut 
700 1 |a Le Deist, Francoise  |e verfasserin  |4 aut 
700 1 |a Hirschfeld, Aaron F  |e verfasserin  |4 aut 
700 1 |a Mitchell, David  |e verfasserin  |4 aut 
700 1 |a Nguyen, Van-Hung  |e verfasserin  |4 aut 
700 1 |a Gagnon, Remi  |e verfasserin  |4 aut 
700 1 |a Mazer, Bruce  |e verfasserin  |4 aut 
700 1 |a Turvey, Stuart E  |e verfasserin  |4 aut 
700 1 |a Jabado, Nada  |e verfasserin  |4 aut 
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